Bones? Heart? Lungs? How are they related?
Morquio A (also called MPS IVA) is an inherited condition that affects major organ systems in the body. People born with Morquio A are missing or don’t make enough of an important enzyme and, as a result, they can’t break down certain materials in the body. These materials eventually build up in tissues, bones, and major organ systems. Morquio A can cause potentially serious problems, including heart disease, skeletal abnormalities, vision and hearing loss, difficulty breathing, and early death.
The more you know about how Morquio A works and what parts of your body it affects, the more power you will have to be your own advocate.
The menu options to the left will help you find out more about Morquio A and the recently published “International Guidelines for the Management and Treatment of Morquio A Syndrome.” Here is what you will find in each section:
What is Morquio A? Find the answer to this question with facts about how Morquio A works. Take a look at this section to understand the science behind Morquio A.
Learn about the early signs of Morquio A, and see the full list of symptoms that go along with the syndrome.
This section is full of information about how Morquio A is diagnosed. Since Morquio A can progress over time, it is important to talk to your doctor about getting a diagnosis as early as possible to prevent more damage to different parts of your body.
Now that you know about Morquio A, find out how VIMIZIM® (elosulfase alfa) enzyme replacement therapy works.
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